Discovery Series: Introduction to Rare Disease:Definition, Examples and Clinical Trial Design from takeaways definition Watch Video

⏲ Duration: 23 min 71 sec
✓ Published: 18-Nov-2014

Description:
Presenter: Pirouz Shamszad, MD - Medical Director, MedpacenPresentation 1 of 3 in Medpace Discovery Series - Rare Disease - Connecting the DotsnnKey takeaways from this presentation are: n nPlanning and executing a study for a Rare Disease is challenging. Major issues exist involving protocol design, patient recruitment and retention, and global regulatory design. n•Best practices to accelerate these novel compounds to commercialization given difficult rare disease and orphan drug studiesn•S